Бомтабегаген бавопарвовец

Rec. INN (наименование, зарегистрированное ВОЗ)

2364477-20-1

recombinant, non-replicating adeno-associated virus serotype 9 (AAV9) vector encoding human lysosomal acid beta-galactosidase (GLB1), under control of a cytomegalovirus immediate early enhancer fused to a chicken beta-actin promoter, a chimeric intron containing splice donor site of the chicken beta-actin intron and splice acceptor site of the rabbit beta-globin gene, and terminated with the simian virus 40 (SV40) polyadenylation sequence, flanked by AAV2 inverted terminal repeats (ITRs).

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